BioMarin updates the Multicenter and Multinational Clinical Study 111-901
The "Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia" is a prospective observational study. This study's code name is 111-901.
The aim of this study is to collect systematic growth measurements of the children in order to collect data to better understand the natural history of achondroplasia.
Children between 2 and 13 years old can be enrolled in the 111-901 study. The measurements take place every 3 months and can go for up to 60 months (or 5 years).
BMN-111 will not be administered in this study. Yet, only children that participate in the study 111-901 can be enrolled in the drug study afterwards, with the code 111-301, in which BMN-111 will be administrated to 50% of participants while the others will receive a placebo.
| Credits: Brakefield R. Observational Studies and Experiments, 2015 |
Locations:
| United States, |
|
| Harbor-UCLA Medical Center | |
| Los Angeles, California, United States, 90048 | |
| Contact: Nathalia Patritti Cressey, Study Coord 310-781-3682 ext Office | |
| Contact 310-597-1960 ext Cell | |
| Principal Investigator: Patti Dickson, MD | |
| Children's Hospital and Research Center Oakland | |
| Oakland, California, United States, 94609 | |
| Contact: Jacqueline Madden, Study Coord 510-428-3885 ext 5745 | |
| This email address is being protected from spambots. You need JavaScript enabled to view it. | |
| Children's Hospital Colorado | |
| Aurora, Colorado, United States, 80045 | |
| Contact: Laurel Ware, BSN 720-777-5378 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Gary Bellus | |
| Nemours/Alfred I. duPont Hospital for Children | |
| Wilmington, Delaware, United States, 19803 | |
| Contact: Cassie Brown, Study Coord 302-298-7930 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Michael Bober, MD | |
| Emory University | |
| Decatur, Georgia, United States, 30033 | |
| Contact: Elizabeth Smith, Study Coord This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: William Wilcox, MD This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Ann and Robert H Lurie Children's Hospital of Chicago | |
| Chicago, Illinois, United States, 60614 | |
| Contact: Victoria Sanders, Study Coord 312-227-6120 | |
| Indiana University, Riley Children's Hospital | |
| Indianapolis, Indiana, United States, 46202 | |
| Contact: Susan Romie 317-278-6650 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: David Weaver, MD | |
| Johns Hopkins McKusick- Institute of Genetic Medicine | |
| Baltimore, Maryland, United States, 21287 | |
| Contact: Adekemi Alade, Study Coord This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Kira Lurman, Study Coord This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| University of Missouri | |
| Columbia, Missouri, United States, 65201 | |
| Contact: Vicki L Jones, Study Coord 573-882-7583 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Daniel G Hoernschemeyer, MD 573-882-1351 | |
| Principal Investigator: Daniel G Hoernschemeyer, MD | |
| Cincinnati Children's Hospital Medical Center | |
| Cincinnati, Ohio, United States, 45229 | |
| Contact: Racheal Powers 800-647-4805 | |
| Principal Investigator: Howard Saal, MD | |
| Vanderbilt University | |
| Nashville, Tennessee, United States, 37232 | |
| Contact: LeeAnna Melton, Study Coord 615-343-6761 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Baylor College of Medicine | |
| Houston, Texas, United States, 77030 | |
| Contact: Catherine Loffredo, Study Coord This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Seattle Children's Hospital | |
| Seattle, Washington, United States, 98105 | |
| Contact: Tressa Mattioli-Lewis This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Klane White, MD This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Klane White, MD | |
| Medical College of Wisconsin, Children's Hospital | |
| Milwaukee, Wisconsin, United States, 53226 | |
| Contact: Paula Engelking 414-266-3289 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Donald Basel, MD This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Donald Basel, MD |
|
| Australia, Victoria | |
| Murdoch Children's Research Institute | |
| Parkville, Victoria, Australia, 3052 |
|
| France | |
| Institut Necker | |
| Paris, France, 75015 | |
| Contact: Kim-Hahn Le Quan Sang, MD 33 1 44 49 59 51 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Valerie Cormier-Daire, MD |
|
| Spain | |
| Institut Catala de Traumatologica I Medicina de l'Esport | |
| Barcelona, Spain, 08028 | |
| Contact: Miriam Perez +34 932 05 43 62 ext 21148 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Ignacio Ginebreda +34 619 21 35 77 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Ignacio Ginebreda | |
| Hospital Sant Joan de Deu Barcelona | |
| Barcelona, Spain, 08950 | |
| Contact: Jose Maria de Bergua +34 650 80 60 71 | |
| Contact: Rosendo Ullot +34 650 80 60 71 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Rosendo Ullot | |
| Hospital Universitario Virgen de la Victoria | |
| Málaga, Spain, 29010 | |
| Contact: Antonio Leiva +34 646 56 87 89 | |
| Contact: Felipe Luna +34 607 85 81 22 | |
| Principal Investigator: Felipe Luna |
|
| Turkey | |
| Acibadem University School of Medicine | |
| Istanbul, Turkey, 34752 | |
| Contact: Beyzanur Gonenc +90 532 300 09 13 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Contact: Burcu Menderes +90 555 313 40 86 This email address is being protected from spambots. You need JavaScript enabled to view it. |
|
| Principal Investigator: Yesemin Alanay, MD | |
| Sub-Investigator: Selda Karaayvaz |
|
| United Kingdom | |
| Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital | |
| London, United Kingdom, SE1 9RT | |
| Principal Investigator: Melita Irving, MD | |
Information available on Clinicaltrials.gov
